Unit 2: Brave New World

6. What is Gene Therapy?

Watch the video and answer the following questions.

a) What is gene therapy used for?

.........................................................................................................................................................................................
b) The medical field this company focuses on is.............................................................................................................
c) How do genes work? Explain......................................................................................................................................
.........................................................................................................................................................................................
d) Fill in the blanks with the missing words:
Many diseases have a................................................, meaning that mutated......................provide
.....................................instructions, that cause the cell to produce an ............................ protein or a
..............................production of protein completely.
e) What is the mutated gene replaced with?.....................................................................................................................
f) What does gene therapy use to deliver genes into cells?.............................................................................................
g) What is AAV and what is it used for?........................................................................................................................
.........................................................................................................................................................................................
h) How does AAV work?.................................................................................................................................................
.........................................................................................................................................................................................
i) Mention two diseases that genetic defects in the eye can cause...................................................................................
j) One inherited retinal disease is mentioned. What is it?...............................................................................................
k) What does it consist of?...............................................................................................................................................

NOW, REACT!
In your opinion, is gene therapy useful? Why? Why not? Justify.

Unit 2: Brave New World

6. What is Gene Therapy?
Watch the video and answer the following questions.

a) What is gene therapy used for?

.........................................................................................................................................................................................
b) The medical field this company focuses on is.............................................................................................................
c) How do genes work? Explain......................................................................................................................................
.........................................................................................................................................................................................
d) Fill in the blanks with the missing words:
Many diseases have a................................................, meaning that mutated......................provide
.....................................instructions, that cause the cell to produce an ............................ protein or a
..............................production of protein completely.
e) What is the mutated gene replaced with?.....................................................................................................................
f) What does gene therapy use to deliver genes into cells?.............................................................................................
g) What is AAV and what is it used for?........................................................................................................................
.........................................................................................................................................................................................
h) How does AAV work?.................................................................................................................................................
.........................................................................................................................................................................................
i) Mention two diseases that genetic defects in the eye can cause...................................................................................
j) One inherited retinal disease is mentioned. What is it?...............................................................................................
k) What does it consist of?...............................................................................................................................................

NOW, REACT!
In your opinion, is gene therapy useful? Why? Why not? Justify.